Type of therapy where healthy genetic code is incorporated into the patient’s body with the goal of treating or preventing disease, reducing further damage and pain or potentially curing the patient. If a mutated gene causes a protein to function poorly, gene therapy may be able to restore the function of the protein.

Precise gene insertion has the potential to overcome limitations of traditional gene therapy that uses adeno-associated virus (AAV) or lenti/retrovirus to deliver genetic code to its target.