Intellia has received a grant from the Bill & Melinda Gates Foundation to develop curative CRISPR/Cas9 in vivo sickle cell disease treatments. Read more.

Funding will be used to develop safe, scalable and accessible non-viral treatments for sickle cell patients.

“My father-in-law, Ben – or as Pam calls him, Benny – lost his battle with AML far too soon, which makes me especially proud to work for a company that is striving to provide curative treatments for that disease, among others.”

Stacey
Associate Director, Finance
Pam, whose husband passed away from acute myeloid leukemia

“Benny had a way of making everything OK. I miss his smile.”

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“UKATPA’s objective is to raise awareness and give support to patients, caregivers and health care professionals.”

Vince
UKATPA Treasurer

Vince and David, friends and colleagues living with ATTR

“The biggest surprise to us was how many people have amyloidosis and don’t have anyone to talk to.”
– David, UKATPA Secretary

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The 2020 Nobel Prize in Chemistry has been awarded “for the development of a method for genome editing.”

Jennifer Doudna, Ph.D.
Co-founder, Intellia Therapeutics

“Have you ever been in an environment full of intellectual people? Now combine that with CRISPR/Cas9. Greatness at full potential.”

Denisse
Sr. Associate Scientist, Mass Spectrometry
Overview

Intellia is a pioneer in the development of CRISPR/Cas9 genome editing and is rapidly moving experimental therapies towards the clinic.

Our company’s unique strengths include our modular lipid nanoparticle delivery system and our determined focus on product development.

Programs & Pipeline

Each one of us together for patients

We believe our modular approach to selecting our in vivo and ex vivo programs positions us to build a full-spectrum genome editing company, with a pipeline across a range of indications. This approach enables us to generate a wealth of data that opens the potential therapeutic applications of the CRISPR/Cas9 technology across a broad range of diseases.

Join Us.
See how you can change life stories with genome editing
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April 13, 2021

#HAE is a rare genetic disorder characterized by recurrent episodes of debilitating and potentially fatal swelling in various parts of the body. Learn more about our approach to treating this condition using #CRISPR/Cas9: https://t.co/skagAH8dyk https://t.co/jEa4mTlqEw

April 12, 2021

#ICYMI Intellia CSO, @LauraSepplore, was recently a guest on @BioAgilytix’s podcast, Molecular Moments, discussing her path from Argentina to the U.S., gene therapy vs. #genomeediting and the work we’re doing at Intellia. Listen here: https://t.co/vnXn2AC4Wd https://t.co/UKS9Jgwn5N

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