Disease Focus

Transthyretin amyloidosis is a rare, rapidly progressive disease caused by a build-up of misfolded transthyretin proteins produced by the liver.

Hereditary angioedema is a rare, hereditary condition associated with frequent episodes or attacks of painful swelling in various parts of the body.

Acute myeloid leukemia is a cancer of the blood and bone marrow. Without immediate treatment, it can spread quickly to other parts of the body.

Alpha-1 antitrypsin (AAT) deficiency is a genetic disease in which the body does not make enough AAT, a protein that protects the lungs and liver.

Hodgkin lymphoma (HL) is a cancer of the lymphatic system, which is part of the immune system. HL starts when there is a change to the DNA of a white blood cell, known as a lymphocyte.