At Intellia, we focus on identifying opportunities that can positively transform the lives of people living with severe and life-threatening conditions. Learn more about the diseases we’re investigating.
Transthyretin amyloidosis is a rare, rapidly progressive disease caused by a build-up of misfolded transthyretin proteins produced by the liver.
Hereditary angioedema is a rare, hereditary condition associated with frequent episodes or attacks of painful swelling in various parts of the body.
Alpha-1 Antitrypsin Deficiency
Alpha-1 antitrypsin (AAT) deficiency is a genetic disease in which the body does not make enough AAT, a protein that protects the lungs and liver.